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Pipeline

Two product engines built on a shared targeted RNA platform.

The same platform approach can support fibrosis programs through fibrosis-targeted LNP technologies, as well as oncology and immunology programs through AOC-based approaches targeting immune-related pathways and traditionally undruggable cancer targets.

Amphorna Biosciences
Program Area Current Focus
Ampho-100 seriesFibrosisFibrosis-targeted LNP programs for MASH/NASH, IPF, CKD, and cardiac fibrosis.
Ampho-200 seriesOncology / ImmunologyAOC programs for autoimmune or undruggable cancer targets.
Program Detail

Two Engines, One Design Logic

01/ 02

Ampho-100 · Fibrosis

Fibrosis-targeted LNPs deliver RNA payloads to disease-relevant tissues, supporting therapeutic approaches for MASH/NASH, idiopathic pulmonary fibrosis (IPF), chronic kidney disease (CKD), and cardiac fibrosis.

02/ 02

Ampho-200 · Oncology / Immunology

AOC-based approaches are being explored for autoimmune diseases and oncology applications targeting traditionally undruggable cancer targets.

Interested in co-development or licensing?